The trial is a phase 1/2 open-label, ascending-dose study of the safety and efficacy of OPGx-LCA5. Recently, the company ...
University of Minnesota Medical School researchers have shown that reducing chronic inflammation can significantly protect against age-related macular degeneration (AMD)-like pathology in preclinical ...
Emerging gene therapy administered through a one-time subretinal injection marks a major milestone for the inherited retinal disease ...
University of Minnesota Medical School researchers have shown that reducing chronic inflammation can significantly protect ...
Vitelliform macular dystrophy, also known as Best disease, is one of a group of vision-robbing conditions called bestrophinopathies that affect children and young adults. Caused by inherited mutations ...
Bestrophinopathy and Vitelliform Macular Dystrophy represent a spectrum of inherited retinal disorders predominantly associated with mutations in the BEST1 gene. These conditions are characterised by ...