Gene therapy can improve vision in young children with AIPL1-associated retinal dystrophy
Researchers from the NIHR Moorfields Biomedical Research Centre and University College London have found that gene therapy improved visual acuity and preserved retinal structure in young children with ...
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MeiraGTx To Advance Gene Therapy For LCA4 Retinal Dystrophy With Positive Phase I/II Results
(MGTX), a clinical-stage genetic medicines company, on Friday announced the progress in its gene therapy program for Leber Congenital Amaurosis 4 or LCA4, a severe retinal dystrophy caused by a ...
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MeiraGTx Announces Positive Results from First-in-Human Study of Gene Therapy for AIPL1-Related Retinal Dystrophy in Young Children
MeiraGTx Holdings plc announced promising results from a first-in-human study published in The Lancet, involving a gene therapy treatment for children with AIPL1-associated retinal dystrophy ...