Amazon S3 on MSN

FDA approves first gene therapy for hearing loss in the US

The US Food and Drug Administration has approved the first-ever gene therapy specifically targeting genetic hearing loss—a ...
Amazon S3 on MSN

First gene therapy for hearing impairment in the US gains FDA approval

The US Food and Drug Administration has granted approval for the inaugural gene therapy aimed at addressing genetic hearing ...

New 'SMArT' platform makes gene editing in hematopoietic stem cells more efficient and safer

A team of researchers led by Luigi Naldini at the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget) has developed a ...

CRISPR Therapeutics vs. Editas Medicine: Which Gene Editing Stock Is a Better Buy in 2026?

One company dominates with an approved therapy, while the other bets on in vivo innovation. See how their financials and risk ...

Voyager Receives FDA IND Clearance for VY1706, First Gene Therapy Approach to Reducing Tau Production in the Brain for Alzheimer’s Disease

Dosing of adults with early Alzheimer’s disease in clinical trial expected H2 2026 - - Comprehensive preclinical program ...

Taysha Gene Therapies: Shortened Timeline Increases The Potential

Taysha Gene Therapies is now a one-drug company, fully reliant on TSHA-102 for Rett syndrome after discontinuing its previous ...

Can gene therapy achieve what decades of heart failure treatment could not — restoring cardiac function?

Cardiac gene therapy was once viewed as a promising breakthrough before high-profile clinical setbacks dampened expectations. Now, advances in gene delivery, viral vectors and molecular targeting are ...

One-time gene editing treatment lowers 'bad' cholesterol by up to 62%

Patients in London have received a pioneering new gene editing therapy that lowers "bad" cholesterol after a single infusion, ...

FDA Approves First-Ever Gene Therapy For Deafness, Opening Door To New Era

In a worldwide first, a one-and-done gene therapy has been approved to treat a form of hereditary deafness. Many of the ...

Biotech Firm MedTherapy Says It Can Cut Gene Therapy Production Time To One Day

A key claim by the company MedTherapy is a major reduction in production timelines. While gene therapies typically take weeks ...
Healthline

Can Gene Therapy Help Cystic Fibrosis?

While gene therapy for cystic fibrosis is still in the research phase, researchers aim to correct the defective gene responsible for the disease. Current research is promising. Cystic fibrosis (CF) is ...