People with spinal muscle atrophy (SMA), an inherited neuromuscular disease ... The findings were published in Nature ...

About Evrysdi Evrysdi is an SMN2-splicing modifier designed to increase functional SMN protein production. With the introduction of a new tablet formulation, Evrysdi now offers an alternative ...

Roche’s Evrysdi tablet receives US FDA approval for the treatment of spinal muscular atrophy: Basel Friday, February 14, 2025, 13:00 Hrs [IST] Roche, announced that the US Food ...

Daily electrical stimulation of certain nerves in the spinal cord appeared to help three people with spinal muscular atrophy ...

For columnist Alyssa Silva, advances in the development of SMA treatments have felt like glimmers of miracles.

Researchers have shown that a spinal cord-stimulating implant, originally used for paralysis, may help restore muscle ...

A new drug-free, minimally invasive intervention targets the root cause of progressive loss of neural function in spinal muscle atrophy (SMA), an inherited neuromuscular disease.

Spinraza treatment does not lead to significant kidney dysfunction in SMA patients with types 1 and 2, a safety and efficacy ...

A Boston-area biopharmaceutical firm has submitted a biologics license application to the FDA for its investigational, fully ...

Three people with a muscle-destroying disease destined to worsen got a little stronger when an implanted device zapped their ...