Investigators who designed a base-editing treatment are planning an "umbrella of umbrellas" trial, while others are developing roadmaps to guide personalized treatments.
Friedreich ataxia is an autosomal-recessive, neurodegenerative disease that primarily affects the nervous system and heart. It was named after Nicolaus Friedreich, a Professor of Medicine in ...
After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA) in the EU. Skyclarys ...
Unpredictable communication and a lack of transparency are eroding the industry’s and the public’s trust. The FDA, experts ...
Friedreich ataxia, an autosomal recessive neurodegenerative disease, is the most common of the inherited ataxias. The recent discovery of the gene that is mutated in this condition,FRDA, has led to ...
Abstract: Cerebellar ataxia (CA) refers to the incoordination of movements of the eyes, speech, trunk, and limbs caused by cerebellar dysfunction. Conventional machine learning (ML) utilizes ...
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