The global Friedreich’s ataxia market is experiencing notable growth, fueled by advancements in genetic research, enhanced diagnostic technologies, and increased awareness of this rare ...

In October, the U.S. Food and Drug Administration (FDA) for the first time ever issued an Emergency Use Authorization (EUA) ...

The FDA has issued an emergency use authorization for lotilaner chewable tablets (Credelio CAT; Elanco Animal Health) for treating New World screwworm (NWS) infestations in cats and kittens. Credelio ...

Design Therapeutics (DSGN) stock gains as RBC upgrades the biotech, citing a catalyst-rich near-term outlook for the company. Read more here.

Artios Pharma, which looking for newer targets that, like PARP inhibitors, affect the way tumors fix themselves, said its ...

Today, Benzinga's options scanner spotted 8 options trades for Biogen. This is not a typical pattern. The sentiment among ...

The Oxford-Harrington Rare Disease Centre ('OHC') today announced the recipients of the 2025 Rare Disease Scholar Award, which advances promising discoveries from academic labs into clinical practice.

Ten scientists selected for second annual award to pursue innovations in gene, RNA, small molecule and cell therapies to treat rare and ultra-rare diseases OXFORD, England ...

The DVLA has confirmed a list of 118 conditions that all motorists must declare to avoid being penalised. This is the ...

Momentum building around tau: expect VY7523 clinical data and VY1706 clinical entry in 2026 - - Sharpened focus on ...

Infectious meningoencephalitis, characterized by inflammation of both the brain and adjacent meninges, is caused by a variety ...

Non-exclusive license providing Solid’s proprietary, next-generation capsid, AAV-SLB101, to Andelyn Biosciences, a ...