Tiffany Fransen's lifelong clumsiness turned out to be a rare neurodegenerative disease. Friedreich’s ataxia leads to muscle ...
An Illinois family pushed for both boys to receive the potentially life changing medical treatment after one was approved and ...
An experimental gene therapy seems to slow the progression of Huntington’s disease by about 75 per cent, and researchers are ...
A new CRISPR approach can control genes without cutting DNA, opening a safer path for treating genetic diseases. A newly developed form of CRISPR at UNSW Sydney points to a safer way of treating ...
Ultragenyx Pharmaceutical said on Monday that late-stage studies showed its drug for a type of genetic bone disease failed to ...
Three start-ups are aiming to create gene-edited babies. Columnist Michael Le Page has no doubt that editing our offspring ...
The first few months of life are a very important period in terms of human development, and at this point, many of the most ...
Shaun Carmichael has polycystic kidney disease. He needs a transplant, and his wife is a match to donate. CIRCLEVILLE, Ohio — ...
This year saw notable progress in head and neck cancers, Huntington's disease, personalized genetic therapy, and heart ...
The parents of 7-week-old Dhruvan Gopi were warned he might not survive the night as specialists converged around his crib at ...
Australian scientists have identified the key genetic drivers behind long COVID, revealing why some people continue to ...
Shaun Carmichael has polycystic kidney disease. He needs a transplant, and his wife is a match to donate. CIRCLEVILLE, Ohio — ...