Jeremy Bray, 29, lives with Spinal Muscular Atrophy, a neurodegenerative disorder that causes the loss of motor neurons and ...
A man who has gradually lost his ability to move most of his muscles said the treatment he’s relying on to slow — and even ...
Family health history is more than just a story—it's a roadmap. As genetics and technology converge, understanding our DNA is ...
Positive CHMP opinion is based on data from the DEVOTE study which evaluated the high dose regimen of nusinersen in treatment ...
In November 2025, Biogen received a positive opinion from the European Medicines Agency's Committee for Medicinal Products for Human Use recommending approval of a high dose nusinersen regimen for 5q ...
Most orphans at the school do not get enough of the essential vitamins and minerals they need from their diet, leading to ...
While court decisions allowing Indian pharma companies to synthesise and market patented drugs, taking into account public ...
A Rivers man born with a rare motor neuron disease causing his muscles to slowly weaken worries his family won’t be able to ...
This brings the number of genetic conditions approved for pre-implantation testing of embryos to 169. Read more at straitstimes.com. Read more at straitstimes.com.
SMA is a rare, genetic neuromuscular condition that affects people across age groups. With treatment landscapes evolving ...
Epirium Bio Inc. (Epirium), a clinical-stage biopharmaceutical company advancing medicines for neuromuscular and fibrotic diseases, presented Phase 1 data for its lead candidate, MF-300, at the ...
On December 3rd, in celebration of the International Day of Persons with Disabilities, the film 'Like Romeo and Juliet' by ...