Inherited retinal dystrophy (IRD) isn’t one disease. It’s many different ones that cause your retina to break down and stop working. They can make you color-blind or night blind. Others can lead to ...
The trial is a phase 1/2 open-label, ascending-dose study of the safety and efficacy of OPGx-LCA5. Recently, the company ...
When I found out I have retinitis pigmentosa (RP), a type of inherited retinal dystrophy, I was shocked. Nobody in my family has vision problems. I had some trouble with my vision, but I thought it ...
Please provide your email address to receive an email when new articles are posted on . The loss of UBAP1L gene function appears to be associated with nonsyndromic retinal dystrophy, according to ...
Emerging gene therapy administered through a one-time subretinal injection marks a major milestone for the inherited retinal disease ...
Clinical Trials Arena on MSN
Opus Genetics doses first subject in gene therapy trial
Opus Genetics has dosed the first subject in its Phase I/II clinical trial of OPGx-Best1 gene therapy for the treatment of ...
Cone rod dystrophy is a rare inherited retinal disorder impacting cones and rods, leading to progressive vision loss. The market for cone rod dystrophy is poised for growth due to rising disease ...
MeiraGTx Holdings plc announced promising results from a first-in-human study published in The Lancet, involving a gene therapy treatment for children with AIPL1-associated retinal dystrophy, ...
(RTTNews) - MeiraGTx Holdings Plc. (MGTX), a clinical-stage genetic medicines company, on Friday announced the progress in its gene therapy program for Leber Congenital Amaurosis 4 or LCA4, a severe ...
This story is part of a series on the current progression in Regenerative Medicine. This piece is part of a series dedicated to the eye and improvements in restoring vision. In 1999, I defined ...
Researchers report that deleting one of the inhibitors of the RPE65 gene in a mouse model that carries a human disease mutation prevents degeneration of cone photoreceptors that are used for daytime ...
Please provide your email address to receive an email when new articles are posted on . The Foundation Fighting Blindness and the Nixon Visions Foundation are working together to launch the Nixon ...
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