As a 4-year-old boy, he was lost on an unfamiliar street in Mumbai, struggling to piece together memories of his family.
In honor of Rare Disease Day on February 28, 2025, we will publish a series of posts throughout the month on As Prescribed ...
The Panhandle Orphan Care Network (POCN) is partnering with the Greater Amarillo Foster Parent Association (GAFPA) to help ...
The Division of Oil and Gas Resources Management has been using drones in Allen, Auglaize, Hancock, Mercer, and Wood counties ...
The US Food and Drug Administration (FDA) has granted orphan drug designation (ODD) and rare paediatric disease designation ...
Ultragenyx Pharmaceutical RARE reported new findings from an ongoing, pivotal study of its investigational candidate, UX111 (ABO-102) AAV gene therapy, for Sanfilippo syndrome type A (MPS IIIA). Per ...
On January 7, 2025, the FDA granted priority review to the new drug application for sunvozertinib (DZD9008), an oral EGFR ...
Ariceum Therapeutics, a private biotech company based in Berlin, has announced that the US Food and Drug Administration (FDA) ...
Each character in The Stone of Madness, including a mute man, an orphan and a woman proficient in witchcraft, has strengths ...
In 1888, struck by the number of orphans she was continuing to find around Atlanta, she founded the Carrie Steele Orphans Home.