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The most common include Leber's hereditary optic neuropathy (LHON), Leigh syndrome, and MELAS (mitochondrial encephalopathy, lactic acidosis, and stroke-like episodes). Depending on which cells are ...

A research team from the Medical University of Vienna and the Medical University of Graz has discovered a previously unknown genetic cause of hereditary optic atrophy, a degenerative disease of the ...

A Prescription Drug User Fee Act target date of February 28, 2026 has been set for the application. The Food and Drug Administration (FDA) has accepted for review the New Drug Application (NDA) for ...

KANSAS CITY, Mo. — Most neuropathies can be successfully treated. Essential Neuropathy is Lee’s Summit looks at the root of the cause, finds treatment methods and helps you get back to living life!

The submission was based on the safety and efficacy data from the phase 3 (RHODOS) and phase 4 (LEROS) studies. The US Food and Drug Administration (FDA) has granted Priority Review to Chiesi Global ...

FDA grants Priority Review to idebenone for Leber Hereditary Optic Neuropathy (LHON), a disease for which there are no existing approved treatments in the U.S.; action date of February 28, 2026 PARMA, ...