KANSAS CITY, Mo. (KCTV) - One resilient metro baby is thriving after a rare genetic disorder diagnosis.
SMA expert Brian Lin, PhD, shares his thoughts on aging with SMA, treatment, advocacy, and supporting patients across their ...
SMA expert Brian Lin, PhD, shares his thoughts on aging with SMA, treatment, advocacy, and supporting patients across their ...
Government data shows that Kerala lowered its Infant Mortality Rate to 5 deaths per 1,000 live births – outpacing even ...
Treatment Market is projected to grow at a healthy rate of around 13% by 2026. This growth is primarily driven by the ...
Treatment with onasemnogene abeparvovec gene therapy for spinal muscular atrophy (SMA) type 1 was associated with less need for nutritional support or nighttime ventilation compared to recommended ...
Spinal muscular atrophy is a rare genetic disease of the nerve cells in the spinal cord that can appear as early as infancy. The disease leads to a progressive loss of muscle strength. Those affected ...
Despite possessing a solid data package on the potential of high-dose Sprinraza in spinal muscular atrophy (SMA), Biogen will now need to revise its application if it hopes to secure an FDA nod. The ...